Huntington’s disease treatment found. Why is it known as world’s most ‘cruel condition’?

Doctors successfully treated Huntington's disease with new gene therapy AMT-130, slowing progression by 75% after 36 months. AMT-130 gene therapy is delivered via brain surgery and a single dose is expected to last a lifetime, offering hope for patients. UniQure plans to submit AMT-130 data to the FDA in early 2026, aiming for approval and launch later that year.